AAV-hAADC gene therapy

Drug Profile

AAV-hAADC gene therapy

Alternative Names: AAV-AADC; AAV-AADC gene therapy; AAV-AADC gene therapy - Voyager Therapeutics; AAV-hAADC-2; AAV2-hAADC; Adeno-associated virus encoding human aromatic L-amino acid decarboxylase (AAV-hAADC-2) - Sanofi Genzyme; AV201; GZ 404477; Parkinson's disease gene therapy-AADC - Sanofi Genzyme; Parkinson's disease gene therapy-AADC - Voyager Therapeutics; VY AADC01

Latest Information Update: 30 Jun 2017

$50 / €47 *
* $ price applies to USA, Canada and Latin America. € price applies to the rest of the world. Final gross prices may vary according to local VAT.

At a glance

  • Originator University of California at San Francisco
  • Developer National Institutes of Health (USA); Sanofi Genzyme; University of California at San Francisco; Voyager Therapeutics
  • Class Antiparkinsonians; Gene therapies
  • Mechanism of Action Dopamine release stimulants; Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

  • New Molecular Entity No

Highest Development Phases

  • Phase I Parkinson's disease

Most Recent Events

  • 30 Jun 2017 Interim adverse events data from a phase I trial in Advanced Parkinson’s Disease released by Voyager Therapeutics
  • 26 Jun 2017 Voyager Therapeutics plans a phase II/III trial for Parkinson’s disease in late 2017
  • 11 May 2017 Voyager Therapeutics initiates enrolment in a phase I trial for Parkinson's Disease in USA (NCT03065192; 9218784)
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