Drug Profile


Alternative Names: 2'-O-methyl-phosphorothioate oligonucleotide; 2402968; GSK-2402968; GSK2402968A; h51AON23; Kyndrisa; PRO-051

Latest Information Update: 10 Sep 2017

Price : *
* Final gross price and currency may vary according to local VAT and billing address.

At a glance

  • Originator Prosensa
  • Developer BioMarin Nederland
  • Class Antisense oligonucleotides
  • Mechanism of Action Dystrophin stimulants; RNA interference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Duchenne muscular dystrophy
  • New Molecular Entity Yes

Highest Development Phases

  • No development reported Duchenne muscular dystrophy

Most Recent Events

  • 15 Dec 2016 Biomarkers information updated
  • 21 Jul 2016 BioMarin Pharmaceuticals completes the phase III Drisapersen confirmatory trial for Duchenne muscular dystrophy (In children, In adolescents) in Belgium (SC) (EudraCT2014-005296-81)
  • 31 May 2016 Discontinued - Phase-III for Duchenne muscular dystrophy in Netherlands, Spain (SC)
Restricted Access

Oops, it looks like you don’t have a valid subscription to this content. To gain full access to the content and functionality of the AdisInsight database try one of the following.

  • with a username/password associated to an account with a valid subscription
  • Contact your organization’s admin about adding this content to your AdisInsight subscription
  • Request a trial

If you are a subscriber to this content then contact us at AsktheExpert.AdisInsight@springer.com so we can help.

Back to top