SAR 422459

Drug Profile

SAR 422459

Alternative Names: ATP-binding transporter gene therapy; SAR422459; Stargardt disease gene therapy - Oxford BioMedica/Sanofi; StarGen

Latest Information Update: 10 Sep 2017

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At a glance

  • Originator Oxford BioMedica
  • Developer Oxford BioMedica; Sanofi
  • Class Gene therapies
  • Mechanism of Action Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Eye disorders
  • New Molecular Entity No

Highest Development Phases

  • Phase I/II Stargardt disease

Most Recent Events

  • 16 Sep 2015 Phase-I/II development is ongoing for Stargardt disease 1 in USA and France (NCT01367444, NCT01736592)
  • 17 Oct 2013 Oxford BioMedica reaches an agreement with the US FDA and ANSM to resume recruitment into the phase I/IIa trial for Stargardt disease 1 in USA and France
  • 03 Jun 2013 Oxford BioMedica suspends enrolment in its phase I/II trial for Stargardt disease 1 in USA (NCT01367444)
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