AMT 060

Drug Profile

AMT 060

Alternative Names: AAV5-hFIX; AMT-060

Latest Information Update: 14 Jul 2017

Price : $50

At a glance

  • Originator Amsterdam Molecular Therapeutics
  • Developer St. Jude Childrens Research Hospital; uniQure; University College London
  • Class Gene therapies
  • Mechanism of Action Factor IX stimulants; Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Haemophilia B
  • New Molecular Entity No

Highest Development Phases

  • Phase I/II Haemophilia B

Most Recent Events

  • 10 Jul 2017 Updated efficacy data from a phase I/II trial in Haemophilia B released by uniQure
  • 25 Apr 2017 AMT 060 receives Priority Medicine (PRIME) status for Haemophilia B in European Union
  • 30 Jan 2017 AMT 060 receives Breakthrough Therapy status for Haemophilia B in USA
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