Drug Profile
Ponatinib - Takeda
Alternative Names: AP-24534; AP24534 HCl; AP24534 hydrochloride; AP24534-HCL; Iclusig; Ponatinib hydrochlorideLatest Information Update: 26 Mar 2024
Price :
$50
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At a glance
- Originator ARIAD Pharmaceuticals
- Developer Dana-Farber Cancer Institute; Fundacion CRIS de Investigacion para Vencer el Cancer; Incyte Biosciences International; Incyte Corporation; Massachusetts General Hospital; Mayo Clinic; National Cancer Institute (USA); Otsuka Beijing Research Institute; Otsuka Pharmaceutical; Takeda; University of Birmingham; University of Colorado at Denver
- Class Antineoplastics; Benzamides; Imidazoles; Piperazines; Pyridazines; Small molecules
- Mechanism of Action Bcr-abl tyrosine kinase inhibitors; Fibroblast growth factor receptor antagonists; Fms-like tyrosine kinase 3 inhibitors; Platelet derived growth factor alpha receptor antagonists; Proto oncogene protein c ret inhibitors; Proto oncogene protein c-kit inhibitors; Vascular endothelial growth factor receptor antagonists
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Marketed Chronic myeloid leukaemia; Precursor cell lymphoblastic leukaemia-lymphoma
- Phase II Acute myeloid leukaemia; Biliary cancer; Gastrointestinal stromal tumours; Lung cancer; Squamous cell cancer; Thyroid cancer
- Phase I/II Haematological malignancies; Solid tumours
Most Recent Events
- 26 Mar 2024 Launched for Precursor cell lymphoblastic leukaemia-lymphoma (Combination therapy) in USA (PO)
- 19 Mar 2024 Registered for Precursor cell lymphoblastic leukaemia-lymphoma (Combination therapy) in USA (PO)
- 09 Dec 2023 Safety and efficacy data from a phase II OPTIC trial in Chronic Myeloid Leukemia presented at the 65th American Society of Hematology Annual Meeting and Exposition (ASH-2023)