Research programme: inherited muscular disorder therapeutics - Retrophin

Drug Profile

Research programme: inherited muscular disorder therapeutics - Retrophin

Alternative Names: RE-001; RE-002; RE-003

Latest Information Update: 28 Nov 2014

Price : $50

At a glance

  • Originator Retrophin
  • Class Recombinant fusion proteins
  • Mechanism of Action Dystrophin stimulants
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

  • New Molecular Entity No

Highest Development Phases

  • Preclinical Duchenne muscular dystrophy
  • Research Congenital structural myopathies; Spinal muscular atrophy

Most Recent Events

  • 28 Nov 2014 Active development for Duchenne muscular dystrophy is ongoing in USA
  • 14 Feb 2013 RE 001 is still in preclinical trials for Duchenne muscular dystrophy in USA (Parenteral)
  • 28 May 2012 Early research in Congenital structural myopathies in USA (unspecified route)
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