Drug Profile


Alternative Names: RE-024

Latest Information Update: 16 Feb 2017

Price : $50

At a glance

  • Originator Retrophin
  • Class Amino acids; Imides; Neuroprotectants; Phosphates; Small molecules; Vitamins
  • Mechanism of Action Phosphopantothenate replacements
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Pantothenate kinase-associated neurodegeneration
  • New Molecular Entity Yes

Highest Development Phases

  • Phase II Pantothenate kinase-associated neurodegeneration

Most Recent Events

  • 16 Feb 2017 CTP push 268553 (NCT03041116) - Planned trial info already updated; Trial identifiers and qualifiers added
  • 24 Jan 2017 Phase-II clinical trials in Pantothenate kinase-associated neurodegeneration in USA (PO) before January 2017 (Retrophin pipeline, January 2017)
  • 02 Jan 2017 Chemical structure information added
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