Drug Profile


Alternative Names: ACT-434964; OGT-923 - Actelion

Latest Information Update: 26 Jul 2016

Price : $50

At a glance

  • Originator Actelion Pharmaceuticals
  • Class Antihyperlipidaemics; Piperidines; Small molecules
  • Mechanism of Action Glucosylceramide synthase inhibitors
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

  • New Molecular Entity Yes

Highest Development Phases

  • Phase I Fabry's disease
  • No development reported Lipid metabolism disorders

Most Recent Events

  • 14 Feb 2017 Actelion plans a phase III trial for Fabry disease
  • 21 Jul 2016 Actelion completes phase Ib trial in Fabry's disease (PO) in Germany
  • 01 Feb 2015 Phase-I clinical trials in Fabry's disease (PO) in Germany
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