Drug Profile


Latest Information Update: 26 Jul 2016

Price : $50

At a glance

  • Originator Actelion Pharmaceuticals
  • Class Antihyperlipidaemics; Piperidines; Small molecules
  • Mechanism of Action Undefined mechanism
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

  • New Molecular Entity Yes

Highest Development Phases

  • Phase I Fabry's disease
  • No development reported Lipid metabolism disorders

Most Recent Events

  • 21 Jul 2016 Actelion completes phase Ib trial in Fabry's disease
  • 30 Jun 2015 Phase-I clinical trials in Fabry's disease (unspecified route) before June 2015
  • 31 Dec 2012 Phase-I clinical trials in Lipid metabolism disorders in Europe (unspecified route)
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