Research programme: RNA targeted therapeutics - RaNA Therapeutics

Drug Profile

Research programme: RNA targeted therapeutics - RaNA Therapeutics

Latest Information Update: 09 May 2016

Price : $50

At a glance

  • Originator RaNA Therapeutics
  • Class Oligonucleotides
  • Mechanism of Action RNA modulators
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

  • On Fast track

    Fast track status is assigned by the US FDA so therapies with the potential to address unmet needs can move faster through development.

  • New Molecular Entity Yes

Highest Development Phases

  • Preclinical Friedreich's ataxia; Spinal muscular atrophy
  • Research Inflammation; Musculoskeletal disorders

Most Recent Events

  • 09 May 2016 RaNA Therapeutics in-licenses RNA technology patent from Massachusetts General Hospital
  • 09 May 2016 RaNA Therapeutics has more that 150 patents pending for transcriptional and post-transcriptional activation platform in USA
  • 09 May 2016 RaNA Therapeutics receives patent allowance for RaNA’s transcriptional activation platform in USA
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