Research programme: recombinant human acid ceramidase - Plexcera Therapeutics

Drug Profile

Research programme: recombinant human acid ceramidase - Plexcera Therapeutics

Alternative Names: Recombinant human acid ceramidase; rhAC; RVT-801

Latest Information Update: 03 Nov 2016

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At a glance

  • Originator Icahn School of Medicine at Mount Sinai
  • Developer Enzyvant Sciences; Plexcera Therapeutics
  • Class Ceramidases
  • Mechanism of Action Acid ceramidase replacements
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Farber lipogranulomatosis
  • New Molecular Entity Yes

Highest Development Phases

  • Preclinical Farber lipogranulomatosis
  • Discontinued Cystic fibrosis

Most Recent Events

  • 02 Aug 2016 Discontinued - Preclinical for Cystic fibrosis in USA (Inhalation)
  • 12 Jul 2016 Preclinical development is ongoing in USA
  • 12 Jul 2016 Enzyvant Sciences announces intention to submit IND applications for clinical trials in Farber disease
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