UX 003

Drug Profile

UX 003

Alternative Names: Recombinant beta-glucuronidase - Ultragenyx; Recombinant human beta glucuronidase; rhGUS; UX-003; UX003-rhGUS

Latest Information Update: 25 Mar 2017

Price : $50

At a glance

  • Originator Saint Louis University
  • Developer Saint Louis University; Ultragenyx Pharmaceutical
  • Class Glucuronidases
  • Mechanism of Action Glucuronidase replacements
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Mucopolysaccharidosis VII
  • New Molecular Entity Yes

Highest Development Phases

  • Phase III Mucopolysaccharidosis VII

Most Recent Events

  • 16 Feb 2017 Ultragenyx announces intention to submit NDA and MAA to USFDA and EMA in the second half of 2017
  • 07 Nov 2016 Ultragenyx was issued composition of matter and method of treatment patent for UX 003 in USA with validity upto 2035
  • 14 Jul 2016 Adverse events and efficacy data from a phase III trial in Mucopolysaccharidosis VII released by Ultragenyx
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