Vestronidase alfa - Ultragenyx Pharmaceutical

Drug Profile

Vestronidase alfa - Ultragenyx Pharmaceutical

Alternative Names: Mepsevii; Recombinant beta-glucuronidase - Ultragenyx; Recombinant human beta glucuronidase; rhGUS; UX-003; Vestronidase alfa - vjbk

Latest Information Update: 17 Nov 2017

Price : *
* Final gross price and currency may vary according to local VAT and billing address.

At a glance

  • Originator Saint Louis University
  • Developer Ultragenyx Pharmaceutical
  • Class Glucuronidases
  • Mechanism of Action Glucuronidase replacements
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Mucopolysaccharidosis VII
  • New Molecular Entity Yes

Highest Development Phases

  • Registered Mucopolysaccharidosis VII

Most Recent Events

  • 15 Nov 2017 Registered for Mucopolysaccharidosis VII (In adolescents, In children, In adults) in USA (IV) - First global approval
  • 15 Nov 2017 Ultragenyx Pharmaceutical receives Rare Pediatric Disease Priority Review Voucher for treatment of Mucopolysaccharidosis VII
  • 23 May 2017 FDA assigns PDUFA action date of 16/11/2017 for vestronidase alfa for Mucopolysaccharidosis VII
Restricted Access

Oops, it looks like you don’t have a valid subscription to this content. To gain full access to the content and functionality of the AdisInsight database try one of the following.

  • with a username/password associated to an account with a valid subscription
  • Contact your organization’s admin about adding this content to your AdisInsight subscription
  • Request a trial

If you are a subscriber to this content then contact us at so we can help.

Back to top