Drug Profile


Alternative Names: AGIL-FA

Latest Information Update: 08 Nov 2017

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At a glance

  • Originator Agilis Biotherapeutics
  • Class Gene therapies
  • Mechanism of Action Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Friedreich's ataxia
  • New Molecular Entity Yes

Highest Development Phases

  • Preclinical Friedreich's ataxia

Most Recent Events

  • 31 Oct 2017 AGIL FA receives Orphan Drug status for Friedreich's ataxia in European Union
  • 03 Oct 2017 Agilis Biotherapeutics announces intention to submit IND application to US FDA for Friedreich's ataxia in 2018
  • 02 Aug 2016 AGIL FA receives Orphan Drug status for Friedreich's ataxia in USA
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