GS 010

Drug Profile

GS 010

Alternative Names: GS010; ND4 gene therapy; rAAV2/2-ND4; RAAV2/2-ND4 vector

Latest Information Update: 01 Aug 2017

Price : *
* Final gross price and currency may vary according to local VAT and billing address.

At a glance

  • Originator GenSight Biologics
  • Class Eye disorder therapies; Gene therapies
  • Mechanism of Action Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Leber's hereditary optic atrophy
  • New Molecular Entity No

Highest Development Phases

  • Phase III Leber's hereditary optic atrophy

Most Recent Events

  • 03 Oct 2017 GenSight Biologics plans a phase III trial for Leber's hereditary optic neuropathy (In children, In adolescents, In adults) (NCT03293524)
  • 01 Aug 2017 GenSight Biologics completes enrolment in the phase III RESCUE trial for Leber's hereditary optic atrophy in France, Germany, Italy, USA and United Kingdom
  • 14 Jun 2017 Efficacy and adverse events data from a phase I/II trial in Leber’s Hereditary Optic Neuropathy released by GenSight Biologics
Restricted Access

Oops, it looks like you don’t have a valid subscription to this content. To gain full access to the content and functionality of the AdisInsight database try one of the following.

  • with a username/password associated to an account with a valid subscription
  • Contact your organization’s admin about adding this content to your AdisInsight subscription
  • Request a trial

If you are a subscriber to this content then contact us at AsktheExpert.AdisInsight@springer.com so we can help.

Back to top