Research programme: haemophilia A gene therapy - uniQure

Drug Profile

Research programme: haemophilia A gene therapy - uniQure

Latest Information Update: 11 Jun 2014

Price : $50

At a glance

  • Originator uniQure
  • Class Gene therapies
  • Mechanism of Action Factor VIII stimulants; Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

  • New Molecular Entity No

Highest Development Phases

  • Preclinical Haemophilia A

Most Recent Events

  • 06 Jun 2014 Preclinical trials in Haemophilia A in Netherlands (Parenteral)
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