Research programme: Charcot-Marie-Tooth disease therapeutics - Charcot-Marie-Tooth Association/Sanofi Genzyme

Drug Profile

Research programme: Charcot-Marie-Tooth disease therapeutics - Charcot-Marie-Tooth Association/Sanofi Genzyme

Latest Information Update: 16 Dec 2016

Price : $50

At a glance

  • Originator Charcot-Marie-Tooth Association; Genzyme Corporation
  • Developer Charcot-Marie-Tooth Association; Sanofi Genzyme
  • Class Small molecules
  • Mechanism of Action Gene expression modulators
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • On Fast track

    Fast track status is assigned by the US FDA so therapies with the potential to address unmet needs can move faster through development.

    No
  • New Molecular Entity Yes

Highest Development Phases

  • Research Charcot-Marie-Tooth disease

Most Recent Events

  • 22 Sep 2014 Early research in Charcot-Marie-Tooth disease in USA (unspecified route)
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