Deflazacort - Marathon Pharmaceuticals

Drug Profile

Deflazacort - Marathon Pharmaceuticals

Alternative Names: 21 desacetyl DFZ prodrug; DFZ; Emflaza; MP-104

Latest Information Update: 06 Oct 2017

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At a glance

  • Originator Marathon Pharmaceuticals
  • Class Anti-inflammatories; Antiallergics; Antiasthmatics; Antipsoriatics; Antirheumatics; Glucocorticoids; Pregnenediones; Small molecules
  • Mechanism of Action Steroid receptor agonists
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Duchenne muscular dystrophy
  • New Molecular Entity Yes

Highest Development Phases

  • Marketed Duchenne muscular dystrophy

Most Recent Events

  • 24 Aug 2017 Marathon Pharmaceuticals completes a long-term extension phase I trial in Duchenne muscular dystrophy (In children, In adolescents) in USA (PO) (NCT02295748)
  • 08 May 2017 PTC Therapeutics plans to launch Deflazacort in USA for Duchenne muscular dystrophy
  • 20 Apr 2017 Deflazacort - Marathon Pharmaceuticals licensed to PTC Therapeutics in USA
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