Drug Profile
Research programme: gene therapies - Synpromics /uniQure
Latest Information Update: 16 Aug 2019
Price :
$50
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At a glance
- Originator uniQure
- Class Gene therapies
- Mechanism of Action Gene stimulants; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Liver disorders