GSK 2696275

Drug Profile

GSK 2696275

Alternative Names: GSK2696275; WAS gene therapy - GlaxoSmithKline/Fondazione Telethon/Ospedale San Raffaele; WAS transduced autologous CD34+ stem cells - GlaxoSmithKline/Fondazione Telethon/Ospedale San Raffaele

Latest Information Update: 10 Dec 2015

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At a glance

  • Originator Fondazione Telethon; GlaxoSmithKline; Ospedale San Raffaele
  • Class Gene therapies; Stem cell therapies
  • Mechanism of Action Gene expression stimulants; Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Wiskott-Aldrich syndrome
  • New Molecular Entity No

Highest Development Phases

  • Phase II Wiskott-Aldrich syndrome

Most Recent Events

  • 05 Dec 2015 Interim adverse events data from a phase I/II trial in Wiskott-Aldrich Syndrome reported by San Raffaele Telethon Institute for Gene Therapy
  • 29 Jul 2015 Phase-II clinical trials in Wiskott-Aldrich syndrome (In adolescents, In children, In infants, In adults) in Italy (IV)
  • 01 Mar 2015 GlaxoSmithKline, Fondazione Telethon and Ospedale San Raffaele complete enrolment in phase I/II trial for Wiskott Aldrich syndrome (In infants, In children, In adolescents, In adults) in Italy (NCT01515462)
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