QR 010

Drug Profile

QR 010

Alternative Names: Antisense oligonucleotide targeting the F508delta mutation of CFTR - ProQR Therapeutics; QR 10; QR-010

Latest Information Update: 23 May 2017

Price : $50

At a glance

  • Originator ProQR Therapeutics
  • Class Oligoribonucleotides
  • Mechanism of Action Cystic fibrosis transmembrane conductance regulator modulators; RNA interference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Cystic fibrosis
  • New Molecular Entity Yes

Highest Development Phases

  • Phase I Cystic fibrosis

Most Recent Events

  • 03 Apr 2017 ProQR has patent protection for QR 010 in USA and European Union
  • 28 Feb 2017 ProQR Therapeutics plans a phase II trial for cystic fibrosis in 2018
  • 16 Nov 2016 Safety and efficacy data from a phase I trial in Cystic fibrosis released by ProQR Therapeutics
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