BLU 554

Drug Profile

BLU 554

Alternative Names: BLU-554

Latest Information Update: 30 Nov 2016

Price : $50

At a glance

  • Originator Blueprint Medicines
  • Class Antineoplastics; Small molecules
  • Mechanism of Action Type 4 fibroblast growth factor receptor antagonists
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Hepatocellular carcinoma
  • New Molecular Entity Yes

Highest Development Phases

  • Phase I Cholangiocarcinoma; Hepatocellular carcinoma

Most Recent Events

  • 15 Dec 2016 Biomarkers information updated
  • 26 Nov 2016 Preliminary efficacy and adverse events data from a phase I trial in Hepatocellular carcinoma and Cholangiocarcinoma released by Blueprint Medicines
  • 28 Sep 2015 BLU 554 receives Orphan Drug status for Hepatocellular carcinoma in USA
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