Research programme: glucosylceramide biobetter - BionaturisAlternative Names: BNT 001
Latest Information Update: 22 Aug 2016
At a glance
- Originator Bionaturis
- Class Glucosidases
- Mechanism of Action Glucosylceramidase replacements
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
On Fast track
Fast track status is assigned by the US FDA so therapies with the potential to address unmet needs can move faster through development.
- New Molecular Entity No
Highest Development Phases
- Discontinued Gaucher's disease type I
Most Recent Events
- 22 Aug 2016 Discontinued for Gaucher's disease type I in Spain (PO)