Research programme: Parkinson's disease gene therapy - ShireAlternative Names: TH/GCH1 Gene Pod
Latest Information Update: 30 Oct 2015
At a glance
- Originator Shire
- Class Gene therapies
- Mechanism of Action GTP cyclohydrolase modulators; Tyrosine hydroxylase modulators
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
On Fast track
Fast track status is assigned by the US FDA so therapies with the potential to address unmet needs can move faster through development.
- New Molecular Entity No
Highest Development Phases
- Preclinical Parkinson's disease
Most Recent Events
- 31 Dec 2014 Preclinical trials in Parkinson's disease in USA (Parenteral)