Drug Profile
Sapropterin repurposed - ETX Pharma
Alternative Names: ETX-101Latest Information Update: 11 Oct 2021
Price :
$50
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At a glance
- Originator University of Texas Medical Branch
- Developer ETX Pharma
- Class Antianaemics; Antihypertensives; Anxiolytics; Nootropics; Pterins; Small molecules; Urologics; Vascular disorder therapies
- Mechanism of Action Phenylalanine hydroxylase stimulants
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Discontinued Diabetic gastroparesis; Gastroparesis
Most Recent Events
- 11 Oct 2021 Discontinued - Phase-III for Diabetic gastroparesis in USA (PO)
- 11 Oct 2021 Discontinued - Phase-III for Gastroparesis in USA (PO)
- 29 Jan 2019 Chemical structure information added