RG 7916

Drug Profile

RG 7916

Alternative Names: RG7916; RO 7034067

Latest Information Update: 13 Jan 2017

Price : $50

At a glance

  • Originator PTC Therapeutics
  • Developer PTC Therapeutics; Roche
  • Class
  • Mechanism of Action Survival of motor neuron 2 protein modulators
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Spinal muscular atrophy
  • On Fast track

    Fast track status is assigned by the US FDA so therapies with the potential to address unmet needs can move faster through development.

  • New Molecular Entity Yes

Highest Development Phases

  • Phase II Spinal muscular atrophy

Most Recent Events

  • 06 Jan 2017 RG 7916 receives Orphan Drug status for Spinal muscular atrophy in USA
  • 05 Jan 2017 Phase-II clinical trials in Spinal muscular atrophy (In infants) in France, Italy (PO)
  • 01 Oct 2016 Phase-II clinical trials in Spinal muscular atrophy (In children, In adolescents, In adults) in Italy (PO) (NCT02908685)
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