AAV-REP1 - NightstaRx

Drug Profile

AAV-REP1 - NightstaRx

Alternative Names: AAV2 REP1; NSR-REP1; rAAV2-REP1; rAAV2.REP1; Recombinant adeno-associated virus expressing REP1

Latest Information Update: 26 Jul 2016

Price : *
* Final gross price and currency may vary according to local VAT and billing address.

At a glance

  • Originator University of Oxford
  • Developer NightstaRx; University of Alberta; University of Miami; University of Oxford
  • Class Eye disorder therapies; Gene therapies
  • Mechanism of Action CHM protein expression stimulants; Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Retinal dystrophies
  • New Molecular Entity No

Highest Development Phases

  • Phase III Retinal dystrophies

Most Recent Events

  • 08 Nov 2017 Nightstar plans a phase III registrational trial of NSR-REP1 for choroideremia in the US, Europe and Canada in the first half of 2018
  • 13 Jul 2016 Phase-III clinical trials in Retinal dystrophies in Finland (Intraocular) (EudraCT2015-003958-41)
  • 12 Nov 2015 Phase-II clinical trials in Retinal dystrophies in USA (Intraocular)
Restricted Access

Oops, it looks like you don’t have a valid subscription to this content. To gain full access to the content and functionality of the AdisInsight database try one of the following.

  • with a username/password associated to an account with a valid subscription
  • Contact your organization’s admin about adding this content to your AdisInsight subscription
  • Request a trial

If you are a subscriber to this content then contact us at AsktheExpert.AdisInsight@springer.com so we can help.

Back to top