AAV-hAADC gene therapy - Agilis/National Taiwan University

Drug Profile

AAV-hAADC gene therapy - Agilis/National Taiwan University

Alternative Names: AADC deficiency gene therapy programme - Agilis; AGIL-AADC

Latest Information Update: 05 Dec 2016

Price : $50

At a glance

  • Originator National Taiwan University
  • Developer Agilis Biotherapeutics; National Taiwan University
  • Class Antiparkinsonians; Gene therapies
  • Mechanism of Action Dopamine release stimulants; Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - CNS disorders
  • New Molecular Entity No

Highest Development Phases

  • Phase II CNS disorders

Most Recent Events

  • 01 Dec 2016 AAV-hAADC gene therapy receives Orphan Drug status for CNS disorders (AADC deficiency) in European Union
  • 17 Nov 2016 AAV-hAADC gene therapy receives Rare Paediatric Disease designation for AADC deficiency in USA
  • 16 Nov 2016 Agilis Biotherapeutics initiates a phase IIb trial in CNS disorders (AADC deficiency) in Taiwan
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