ABO 102

Drug Profile

ABO 102

Alternative Names: AAV SGSH; AAV SGSH - Abeona; AAV9 SGSH - Abeona; ABO-102 - Abeona; ABX 102 - Abeona; ABX B - Abeona; SC AAV9 SGSH; scAAV9 SGHG

Latest Information Update: 27 Oct 2016

Price : $50

At a glance

  • Originator Nationwide Children's Hospital
  • Developer Abeona Therapeutics
  • Class Gene therapies
  • Mechanism of Action Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Mucopolysaccharidosis III
  • New Molecular Entity Yes

Highest Development Phases

  • Phase I/II Mucopolysaccharidosis III

Most Recent Events

  • 25 Oct 2016 ABO 102 receives Fast Track designation for Mucopolysaccharidosis III in USA (IV,Injection)
  • 20 Oct 2016 Efficacy and adverse events data from a phase I/II trial in Mucopolysaccharidosis III released by Abeona Therapeutics
  • 18 Oct 2016 ABO 102 receives Orphan Drug status for Mucopolysaccharidosis III in European Union
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