Research programme- ear disorder gene therapies - Applied Genetic Technologies Corporation
Latest Information Update: 22 Aug 2016
At a glance
- Originator Applied Genetic Technologies Corporation
- Class Gene therapies
- Mechanism of Action Undefined mechanism
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
On Fast track
Fast track status is assigned by the US FDA so therapies with the potential to address unmet needs can move faster through development.
- New Molecular Entity Yes
Highest Development Phases
- Research Deafness