Research programme: gene editing therapeutics - Intellia Therapeutics

Drug Profile

Research programme: gene editing therapeutics - Intellia Therapeutics

Alternative Names: CRISPR/Cas9 gene editing therapies - Intellia Therapeutics

Latest Information Update: 19 Apr 2017

Price : $50

At a glance

  • Originator Intellia Therapeutics
  • Class Gene therapies
  • Mechanism of Action Gene modulators
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity No

Highest Development Phases

  • Preclinical Alpha 1-antitrypsin deficiency; Hepatitis B; Inborn error metabolic disorders; Primary hyperoxaluria

Most Recent Events

  • 13 Apr 2017 University of California, University of Vienna, and Charpentier appeals decision by PTAB, which dismissed interference proceedings against Broad Institute, MIT, and Harvard University for a patent related to CRISPR-Cas9 genome editing technology, in USA
  • 04 Apr 2017 CRISPR Therapeutics, Intellia Therapeutics, Caribou Biosciences and ERS Genomics signs a global agreement on the foundational intellectual property for CRISPR-Cas9 gene editing technology
  • 28 Mar 2017 The European Patent Office announces its intention to grant a patent for CRISPR-Cas9 genome editing technology to University of California, University of Vienna, and Charpentier
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