Sodium phenylbutyrate - GMP-Orphan

Drug Profile

Sodium phenylbutyrate - GMP-Orphan

Alternative Names: Satisma

Latest Information Update: 07 Nov 2016

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At a glance

  • Originator GMP-Orphan SAS
  • Class Antineoplastics; Electrolytes; Phenylbutyrates; Small molecules
  • Mechanism of Action Histone deacetylase inhibitors
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Spinal muscular atrophy
  • New Molecular Entity No

Highest Development Phases

  • Clinical Phase Unknown Spinal muscular atrophy

Most Recent Events

  • 07 Nov 2016 Chemical structure information added
  • 03 Jul 2014 GMP-Orphan has published patent for phenyl butyrate for a motor neuron disease or a metabolic disease in USA
  • 22 Jun 2012 Preclinical trials in Spinal muscular atrophy (In adolescents, In children, In infants) in France (unspecified route) after June 2012
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