Factor VII gene therapy - Howard Hughes Medical Institute/Amarna TherapeuticsAlternative Names: SVFVIIa
Latest Information Update: 25 Nov 2016
At a glance
- Originator Amarna Therapeutics; Howard Hughes Medical Institute
- Class Blood coagulation factors; Gene therapies
- Mechanism of Action Gene transference
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
On Fast track
Fast track status is assigned by the US FDA so therapies with the potential to address unmet needs can move faster through development.
- New Molecular Entity No
Highest Development Phases
- Preclinical Haemophilia