AT 342

Drug Profile

AT 342

Alternative Names: AAV-gene-therapy-Audentes; AAV-UGT1A1; AT-342; Crigler-Najjar-Syndrome-gene-therapy-Audentes

Latest Information Update: 16 Nov 2017

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At a glance

  • Originator Audentes Therapeutics
  • Class Gene therapies
  • Mechanism of Action Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Hyperbilirubinaemia
  • New Molecular Entity No

Highest Development Phases

  • Phase I/II Hyperbilirubinaemia

Most Recent Events

  • 13 Nov 2017 The Medicines and Healthcare Products Regulatory Agency approves IND application for the phase I/II VALENS trial of AT 342 in Hyperbilirubinaemia
  • 08 Sep 2017 Phase-I/II clinical trials in Hyperbilirubinaemia (In infants, In children, In adolescents, In adults, In the elderly) in USA (IV) (NCT03223194)
  • 01 Feb 2017 Preclinical trials in Hyperbilirubinaemia in USA (unspecified route)
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