A Controlled N-of-1 Before-and-after Study to Determine Safety and Efficacy Triheptanoin in Patients With Glucose Transporter 1 Deficiency Syndrome

Trial Profile

A Controlled N-of-1 Before-and-after Study to Determine Safety and Efficacy Triheptanoin in Patients With Glucose Transporter 1 Deficiency Syndrome

Active, no longer recruiting
Phase of Trial: Phase II

Latest Information Update: 08 Aug 2016

At a glance

  • Drugs Triheptanoin (Primary)
  • Indications De Vivo disease
  • Focus Therapeutic Use
  • Most Recent Events

    • 08 Aug 2016 According to an Ultragenyx Pharmaceutical media release, data from this study is expected in the second half of 2016.
    • 30 May 2016 Status changed from recruiting to active, no longer recruiting.
    • 01 Dec 2015 Planned End Date changed from 1 Sep 2015 to 1 Feb 2016, according to ClinicalTrials.gov record.
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