Long-term Follow-up of Patients With Sanfilippo Type A Syndrome Who Have Previously Been Treated in the P1-SAF-301 Clinical Study Evaluating the Tolerability and Safety of the Intracerebral Administration of SAF-301 [EXTENSION OF 700240974]

Trial Profile

Long-term Follow-up of Patients With Sanfilippo Type A Syndrome Who Have Previously Been Treated in the P1-SAF-301 Clinical Study Evaluating the Tolerability and Safety of the Intracerebral Administration of SAF-301 [EXTENSION OF 700240974]

Completed
Phase of Trial: Phase I/II

Latest Information Update: 22 Jun 2017

At a glance

  • Drugs SAF 301 (Primary)
  • Indications Mucopolysaccharidosis III
  • Focus Adverse reactions
  • Sponsors LYSOGENE
  • Most Recent Events

    • 19 Jun 2017 Status changed from active, no longer recruiting to completed.
    • 17 Jan 2017 Planned End Date changed from 1 Jul 2016 to 1 Jul 2017.
    • 17 Jan 2017 Planned primary completion date changed from 1 May 2016 to 1 May 2017.
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