A Phase 1 Study Evaluating Gene Therapy by Transplantation of Autologous CD34+ Stem Cells Transduced Ex Vivo With the LentiGlobin BB305 Lentiviral Vector in Subjects With Severe Sickle Cell Disease

Trial Profile

A Phase 1 Study Evaluating Gene Therapy by Transplantation of Autologous CD34+ Stem Cells Transduced Ex Vivo With the LentiGlobin BB305 Lentiviral Vector in Subjects With Severe Sickle Cell Disease

Recruiting
Phase of Trial: Phase I

Latest Information Update: 12 Dec 2017

At a glance

  • Drugs BB305 beta-globin gene therapy bluebird bio (Primary)
  • Indications Sickle cell anaemia
  • Focus Adverse reactions
  • Sponsors bluebird bio
  • Most Recent Events

    • 12 Dec 2017 Results assessing haematopoietic stem cells mobilization with plerixafor alone presented at the 59th Annual Meeting and Exposition of the American Society of Hematology
    • 12 Dec 2017 Interim results presented at the 59th Annual Meeting and Exposition of the American Society of Hematology.
    • 10 Dec 2017 Interim results presented in a bluebird bio Media Release.
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