Trial Profile
A Multicenter Study to Evaluate and Characterize the Effects of Pharmacological Chaperones in Cell Lines Derived From Blood and Skin Samples From Patients With Pompe Disease
Status:
Completed
Phase of Trial:
Phase II
Latest Information Update: 22 May 2014
Price :
$35
*
At a glance
- Drugs Duvoglustat (Primary)
- Indications Glycogen storage disease type II
- Focus Pharmacodynamics
- Sponsors Amicus Therapeutics
- 22 May 2014 New trial record