Trial Profile
An Extension Study of Intrathecal Enzyme Replacement Therapy for Spinal Cord Compression in Mucopolysaccharidosis I [EXTENSION OF 700245412]
Status:
Discontinued
Phase of Trial:
Phase I
Latest Information Update: 06 Nov 2021
Price :
$35
*
At a glance
- Drugs Laronidase (Primary)
- Indications Lysosomal storage diseases; Mucopolysaccharidosis I
- Focus Adverse reactions
- 05 Jun 2014 New trial record