Phase I Gene Transfer Clinical Trial for Spinal Muscular Atrophy Type 1 Delivering AVXS-101

Trial Profile

Phase I Gene Transfer Clinical Trial for Spinal Muscular Atrophy Type 1 Delivering AVXS-101

Completed
Phase of Trial: Phase I

Latest Information Update: 03 Oct 2017

At a glance

  • Drugs AVXS 101 (Primary)
  • Indications Spinal muscular atrophy
  • Focus Adverse reactions; Therapeutic Use
  • Sponsors AveXis
  • Most Recent Events

    • 03 Oct 2017 Top-line data as of August 7, 2017 will be presented at the 22nd International Annual Congress of the World Muscle Society (WMS), according to an AveXis media release. A manuscript regarding these data has been accepted for publication in a major medical journal.
    • 03 Oct 2017 Top-line data as of August 7, 2017 presented in ann AveXis media release.
    • 21 Jul 2017 Planned End Date changed from 1 Dec 2017 to 1 Jan 2018.
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