Clinical phase II trial to compare Treosulfan-based conditioning therapy with Busulfan-based conditioning prior to allogeneic haematopoietic stem cell transplantation (HSCT) in paediatric patients with non-malignant diseases
Phase of Trial: Phase II
Latest Information Update: 28 Jul 2017
At a glance
- Drugs Treosulfan (Primary) ; Busulfan
- Indications Haemoglobinopathies; Immunodeficiency disorders; Inborn error metabolic disorders
- Focus Therapeutic Use
- Sponsors Medac
- 11 Jul 2017 The trial has been completed in Austria.
- 05 Apr 2017 Planned End Date changed from 1 Mar 2019 to 1 Dec 2019.
- 05 Apr 2017 Planned primary completion date changed from 1 Mar 2017 to 1 Dec 2018.