Hydroxypropyl Beta Cyclodextrin for Niemann-Pick Type C1 Disease
Phase of Trial: Phase I/II
Latest Information Update: 10 Aug 2017
At a glance
- Drugs Hydroxypropyl betadex (Primary)
- Indications Niemann-Pick disease type C
- Focus Pharmacokinetics
- Sponsors Vtesse
- 10 Aug 2017 Safety and efficacy results published in The Lancet.
- 10 Jun 2017 Biomarkers information updated
- 18 Apr 2017 Status changed from active, no longer recruiting to completed.