Pivotal trial of AVXS 101 in patients with spinal muscular atrophy type 1
Phase of Trial: Phase II
Latest Information Update: 14 Jun 2017
At a glance
- Drugs AVXS 101 (Primary)
- Indications Spinal muscular atrophy
- Focus Therapeutic Use
- 14 Jun 2017 According to an AveXis media release, this trial is expected to begin in the third quarter of 2017.
- 01 Nov 2016 According to Avexis media release, this trial will reflect single-arm design and use natural history of the disease as a comparator.
- 12 May 2016 According to AveXis media release, the company will initiate the pivotal trials of AVXS-101 in the United States and Europe in the first half of 2017.