Pivotal trial of AVXS 101 in patients with spinal muscular atrophy type 1

Trial Profile

Pivotal trial of AVXS 101 in patients with spinal muscular atrophy type 1

Planning
Phase of Trial: Phase II

Latest Information Update: 14 Jun 2017

At a glance

  • Drugs AVXS 101 (Primary)
  • Indications Spinal muscular atrophy
  • Focus Therapeutic Use
  • Most Recent Events

    • 14 Jun 2017 According to an AveXis media release, this trial is expected to begin in the third quarter of 2017.
    • 01 Nov 2016 According to Avexis media release, this trial will reflect single-arm design and use natural history of the disease as a comparator.
    • 12 May 2016 According to AveXis media release, the company will initiate the pivotal trials of AVXS-101 in the United States and Europe in the first half of 2017.
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