An Open Label, Multi-centre, Phase I/II Dose Escalation Trial of a Recombinant Adeno-associated Virus Vector (AAV2/8-hCARp.hCNGB3) for Gene Therapy of Adults and Children With Achromatopsia Owing to Defects in CNGB3

Trial Profile

An Open Label, Multi-centre, Phase I/II Dose Escalation Trial of a Recombinant Adeno-associated Virus Vector (AAV2/8-hCARp.hCNGB3) for Gene Therapy of Adults and Children With Achromatopsia Owing to Defects in CNGB3

Recruiting
Phase of Trial: Phase I/II

Latest Information Update: 03 May 2017

At a glance

  • Drugs AAV CNGB3 (Primary)
  • Indications Colour vision defects
  • Focus Adverse reactions; First in man
  • Acronyms CNGB3
  • Sponsors MeiraGTx
  • Most Recent Events

    • 08 Feb 2017 According to a MeiraGTx media release, first patient was treated with AAV-mediated gene therapy for achromatopsia due to mutations in the CNGB3 gene
    • 24 Jan 2017 Status changed from not yet recruiting to recruiting.
    • 29 Dec 2016 New trial record
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