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A Phase 2 Randomized, Double-Blind, Placebo-Controlled Study of ACE-083 in Patients With Charcot-Marie-Tooth Disease Types 1 and X

Trial Profile

A Phase 2 Randomized, Double-Blind, Placebo-Controlled Study of ACE-083 in Patients With Charcot-Marie-Tooth Disease Types 1 and X

Status: Discontinued
Phase of Trial: Phase II

Latest Information Update: 24 May 2023

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At a glance

  • Drugs Efmitermant alfa (Primary)
  • Indications Charcot-Marie-Tooth disease
  • Focus Adverse reactions; Therapeutic Use
  • Sponsors Acceleron Pharma
  • Most Recent Events

    • 11 May 2022 Results published in the Neurology
    • 01 May 2020 Results evaluating the effects of ACE-083 injected into the tibialis anterior (TA) muscles of subjects with CMT1 or CMTX and mild-moderate ankle dorsiflexion weakness presented at the 72nd Annual Meeting of the American Academy of Neurology
    • 09 Mar 2020 According to an Acceleron Pharma media release, Acceleron plans to present results of this study at the American Academy of Neurology Annual Meeting in April
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