Trial Profile
A PHASE 1B MULTICENTER, OPEN-LABEL, SINGLE ASCENDING DOSE STUDY TO EVALUATE THE SAFETY AND TOLERABILITY OF PF-06939926 IN AMBULATORY SUBJECTS WITH DUCHENNE MUSCULAR DYSTROPHY
Status:
Active, no longer recruiting
Phase of Trial:
Phase I
Latest Information Update: 14 Dec 2022
Price :
$35
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At a glance
- Drugs Fordadistrogene-movaparvovec (Primary)
- Indications Duchenne muscular dystrophy
- Focus Adverse reactions; First in man; Proof of concept
- Sponsors Pfizer
- 09 Nov 2022 Results investigating the impact fordadistrogene movaparvovec on physical functioning based on the Pediatric Outcomes Data Collection Instrument (PODCI), presented at the 25th Annual European Congress of the International Society for Pharmacoeconomics and Outcomes Research
- 26 Apr 2022 Planned End Date changed from 30 May 2026 to 30 Mar 2026.
- 30 Mar 2022 Planned End Date changed from 15 May 2028 to 30 May 2026.