A Single Arm, Open Label, Clinical Study of Cryopreserved Autologous CD34+ Cells Transduced With Lentiviral Vector Containing Human ARSA cDNA (GSK2696274), for the Treatment of Early Onset Metachromatic Leukodystrophy (MLD)

Trial Profile

A Single Arm, Open Label, Clinical Study of Cryopreserved Autologous CD34+ Cells Transduced With Lentiviral Vector Containing Human ARSA cDNA (GSK2696274), for the Treatment of Early Onset Metachromatic Leukodystrophy (MLD)

Recruiting
Phase of Trial: Phase III

Latest Information Update: 10 Jan 2018

At a glance

  • Drugs GSK 2696274 (Primary)
  • Indications Metachromatic leukodystrophy
  • Focus Therapeutic Use
  • Sponsors GlaxoSmithKline
  • Most Recent Events

    • 10 Jan 2018 New trial record
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