Deferiprone - Apotex
Alternative Names: CGP 37391; CMX 001 - CorMedix; CP 020; CP 20; CRMD-001; FERRIPROX; Ferriprox; Ferriprox Oral Solution; Kelfer; L1; UpkanzLatest Information Update: 04 Apr 2023
At a glance
- Originator Royal Free and University College Medical School
 - Developer Apotex; Centre Hospitalier Univeristaire De Lille; Chiesi; CorMedix
 - Class Antianaemics; Antirheumatics; Pyridones; Small molecules
 - Mechanism of Action Chelating agents
 
- 
          
            
              Orphan Drug Status
              Yes - Siderosis; Friedreich's ataxia; Iron overload; Neurodegenerative disorders
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
 - New Molecular Entity Yes
 
Highest Development Phases
- Marketed Iron overload
 - Phase III Pantothenate kinase-associated neurodegeneration
 - Phase II Amyotrophic lateral sclerosis; Parkinson's disease
 - Phase I/II Friedreich's ataxia
 - No development reported HIV infections
 - Discontinued Kidney disorders