Nitisinone - Swedish Orphan Biovitrum
Alternative Names: NTBC; Orfadin; SC 0735; SYN-118Latest Information Update: 12 Apr 2024
At a glance
- Originator Syngenta
- Developer Biotie Therapies Corp.; Swedish Orphan Biovitrum
- Class Antiparkinsonians; Cyclohexanones; Nitrobenzoates; Small molecules
- Mechanism of Action 4-hydroxyphenylpyruvate dioxygenase inhibitors; Dopamine release stimulants
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Marketed Inborn error metabolic disorders; Tyrosinaemia type I
- Discontinued Parkinson's disease