Drug Profile
Betaine - Recordati
Alternative Names: Betaine-anhydrous; Cystadan; Cystadane; RM-003Latest Information Update: 19 Sep 2022
Price :
$50
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At a glance
- Originator Orphan Medical
- Developer Recordati; ReqMed
- Class Quaternary ammonium compounds; Small molecules; Trimethyl ammonium compounds
- Mechanism of Action Methyltransferase stimulants
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Marketed Homocystinuria
- Discontinued Infantile Refsum disease; Peroxisomal disorders; Zellweger syndrome