Drug Profile
Cystic fibrosis gene therapy - CFTR-cationic lipid complex
Alternative Names: CFTR gene-cationic lipid complex; CFTR gene-cytofectin complex; Cystic fibrosis gene therapy - CFTR-cytofectin complexLatest Information Update: 14 Sep 2022
Price :
$50
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At a glance
- Originator Genzyme Corporation
- Developer Fresh Tracks Therapeutics
- Class Gene therapies
- Mechanism of Action Cystic fibrosis transmembrane conductance regulator stimulants; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Discontinued Cystic fibrosis